FDA approves first oral drug for thalassemia anemia, offering new hope beyond blood transfusions
The US FDA has approved the drug Mitapivat, marketed as Aqvesme, as the very first oral therapy for anemia in adults with alpha or beta thalassemia. This breakthrough offers new hope to patients reliant on frequent blood transfusions for decades. What is thalassemia? Thalassemia is a genetic blood disorder wherein the body cannot make enough…